06 Feb, 2019 Phase 1 Results for Givosiran Published in “The New England Journal of Medicine”
We published results from the Phase 1 study of givosiran, our investigational RNAi therapeutic for the treatment of acute hepatic porphyria (AHP), in The New England Journal of Medicine (NEJM) in a paper titled “Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria.”
Read the paper in The New England Journal of Medicine (more…)