Nonclinical Results Exploring the Utility of RNAi and REVERSIR Technology in Modulating AAV Transgene Expression Published in Nature Communications

Nonclinical Results Exploring the Utility of RNAi and REVERSIR Technology in Modulating AAV Transgene Expression Published in Nature Communications

Results from nonclinical work investigating the potential utility of combining RNAi-mediated knockdown with REVERSIR-enabled rescue of transgene expression as a rheostat for adeno-associated virus (AAV) -delivered genes in the setting of gene therapy were published in the journal Nature Communications.

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